We don’t follow footsteps. We create the path.

Scientist working in Spark's labs in Philadelphia

News & events

Spark Therapeutics Announces Preliminary Data on SPK-8016 Preliminary data presented on Phase 1/2 clinical trial of investigational SPK-8016 in hemophilia A at EAHAD 2021

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Spark Therapeutics Announces First Participant Dosed in Phase 1/2 trial of SPK-3006 First participant dosed in the RESOLUTESM trial, a Phase 1/2 dose-escalation study of investigational SPK-3006 for late-onset Pompe disease

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Spark Therapeutics Announces Updated Data on SPK-8011 Updated data presented on Phase 1/2 clinical trial of investigational SPK-8011 in hemophilia A at ISTH 2020

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We don’t follow footsteps. We create the path.

Our mission at Spark Therapeutics is to unlock the power of gene therapy to accelerate healthcare transformation. We have built a fully integrated company, combining our proprietary adeno-associated viral (AAV) gene therapy platform with excellence in R&D, manufacturing and commercial operations. Find out more about how we strive to turn genes into medicines for patients with inherited diseases, including inherited retinal diseases (IRDs), liver-directed diseases such as hemophilia, and neurodegenerative diseases.

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